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Charlotte Charity Inspires New Law Designed to Spur Treatments for Rare Diseases and Economic Growth for North Carolina
Law Will Establish an Advisory Council on Rare Diseases at the University of North Carolina at Chapel Hill
Located in News / 2015 / August
New gene therapy proves promising as hemophilia treatment
Researchers package specialized blood platelets with genes that express clotting factor, leading to fewer bleeding events.
Located in News / 2013 / December
Newly designed viral vectors could lead to improved gene therapies
UNC and University of Florida researchers created viruses to deliver gene therapies while evading pre-existing immune system responses. Aravind Asokan, PhD, led the research team at UNC.
Located in News / 2017 / June
Promising results with new gene therapy approach for treating inherited neurodegenerative diseases
Approach developed in part by UNC’s Dr. Steven Gray restored enzyme function and extended survival time in treated mice.
Located in News / 2016 / July