The National Hemophilia Foundation (NHF) has honored Paul Monahan, MD, associate professor pediatrics at the UNC School of Medicine, with its Leadership in Research Award for his achievements investigating adeno-associated virus (AAV) vectors in gene therapy for factor IX deficiency. The award will be presented to him June 12 at the foundation’s 65th anniversary reception at the Lighthouse Chelsea Piers in New York City.
NHF established its Leadership in Research Award to recognize the outstanding achievements of researchers and physicians working to improve treatments for hemophilia and advance the field of bleeding disorders research. Dr. Monahan’s research was instrumental in building a better understanding of the potential to safely achieve increased factor IX expression using AAV vectors. The current advances in novel technologies for hemophilia and late-phases human gene therapy trials already underway for patients with factor IX deficiency were made possible through the work of Monahan and others to firmly establish the use of recombinant AAV in animal models.
Read the full announcement from the National Hemophilia Foundation here.